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Chemical Structure| 159351-69-6 Chemical Structure| 159351-69-6

Structure of Everolimus
CAS No.: 159351-69-6

Chemical Structure| 159351-69-6

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Everolimus (RAD001) is a derivative of Rapamycin and a potent, selective, orally active mTOR1 inhibitor. It binds to FKBP-12 to form an immunosuppressive complex, inhibiting tumor cell proliferation, inducing cell apoptosis and autophagy, and exhibiting strong immunosuppressive and anticancer activities.

Synonyms: RAD001; SDZ-RAD; Certican

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Andressa Santana Santos ; Vinícius Alexandre Fiaia Costa ; Vivianny Aparecida Queiroz Freitas ; Laura Raniere Borges dos Anjos ; Eder Soares de Almeida Santos ; Thales Domingos Arantes , et al.

Abstract: Sporotrichosis is recognized as the predominant subcutaneous mycosis in South America, attributed to pathogenic species within the Sporothrix genus. Notably, in Brazil, Sporothrix brasiliensis emerges as the principal species, exhibiting significant sapronotic, zoonotic and enzootic epidemic potential. Consequently, the discovery of novel therapeutic agents for the treatment of sporotrichosis is imperative. The present study is dedicated to the repositioning of pharmaceuticals for sporotrichosis therapy. To achieve this goal, we designed a pipeline with the following steps: (a) compilation and preparation of Sporothrix genome data; (b) identification of orthologous proteins among the species; (c) identification of homologous proteins in publicly available drug-target databases; (d) selection of Sporothrix essential targets using validated genes from Saccharomyces cerevisiae; (e) molecular modeling studies; and (f) experimental validation of selected candidates. Based on this approach, we were able to prioritize eight drugs for in vitro experimental validation. Among the evaluated compounds, everolimus and bifonazole demonstrated minimum inhibitory concentration (MIC) values of 0.5 µg/mL and 4.0 µg/mL, respectively. Subsequently, molecular docking studies suggest that bifonazole and everolimus may target specific proteins within S. brasiliensis– namely, sterol 14-α-demethylase and serine/threonine-protein kinase TOR, respectively. These findings shed light on the potential binding affinities and binding modes of bifonazole and everolimus with their probable targets, providing a preliminary understanding of the antifungal mechanism of action of these compounds. In conclusion, our research advances the understanding of the therapeutic potential of bifonazole and everolimus, supporting their further investigation as antifungal agents for sporotrichosis in prospective hit-to-lead and preclinical investigations.

Keywords: Sporotrichosis ; Sporothrix brasiliensis ; Drug repurposing ; Structural bioinformatics ; Everolimus

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Leclercq, Gabrielle ; Haegel, Hélène ; Toso, Alberto ; Zimmermann, Tina ; Green, Luke ; Steinhoff, Nathalie , et al.

Abstract: Background: T cell engaging therapies, like chimeric antigen receptor T cells and T cell bispecific antibodies (TCBs), efficiently redirect T cells towards tumor cells, facilitating the formation of a cytotoxic synapse and resulting in subsequent tumor cell killing, a process that is accompanied by the release of cytokines. Despite their promising efficacy in the clinic, treatment with TCBs is associated with a risk of cytokine release syndrome (CRS). The aim of this study was to identify small molecules able to mitigate cytokine release while retaining T cell-mediated tumor killing. Methods: By screening a library of 52 Food and Drug Administration approved kinase inhibitors for their impact on T cell proliferation and cytokine release after CD3 stimulation, we identified mTOR, JAK and Src kinases inhibitors as potential candidates to modulate TCB-mediated cytokine release at pharmacologically active doses. Using an in vitro model of target cell killing by human peripheral blood mononuclear cells, we assessed the effects of mTOR, JAK and Src kinase inhibitors combined with 2+1 T cell bispecific antibodies (TCBs) including CEA-TCB and CD19-TCB on T cell activation, proliferation and target cell killing measured by flow cytometry and cytokine release measured by Luminex. The combination of mTOR, JAK and Src kinase inhibitors together with CD19-TCB was evaluated in vivo in non-tumor bearing stem cell humanized NSG mice in terms of B cell depletion and in a lymphoma patient-derived xenograft (PDX) model in humanized NSG mice in terms of antitumor efficacy. Results: The effect of Src inhibitors differed from those of mTOR and JAK inhibitors with the suppression of CD19-TCB-induced tumor cell lysis in vitro, whereas mTOR and JAK inhibitors primarily affected TCB-mediated cytokine release. Importantly, we confirmed in vivo that Src, JAK and mTOR inhibitors strongly reduced CD19-TCB-induced cytokine release. In humanized NSG mice, continuous treatment with a Src inhibitor prevented CD19-TCB-mediated B cell depletion in contrast to mTOR and JAK inhibitors, which retained CD19-TCB efficacy. Ultimately, transient treatment with Src, mTOR and JAK inhibitors minimally interfered with antitumor efficacy in a lymphoma PDX model. Conclusions: Taken together, these data support further evaluation of the use of Src, JAK and mTOR inhibitors as prophylactic treatment to prevent occurrence of CRS.

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Alternative Products

Product Details of Everolimus

CAS No. :159351-69-6
Formula : C53H83NO14
M.W : 958.22
SMILES Code : O=C(N1CCCC[C@H]1C(O[C@H]([C@@H](C[C@H]2C[C@H]([C@@H](CC2)OCCO)OC)C)CC([C@@H](/C=C([C@H]([C@H]3OC)O)\C)C)=O)=O)C([C@@]4(O)[C@@H](CC[C@@H](C[C@@H](/C(C)=C/C=C/C=C/[C@H](C[C@H](C3=O)C)C)OC)O4)C)=O
Synonyms :
RAD001; SDZ-RAD; Certican
MDL No. :MFCD00929329

Safety of Everolimus

GHS Pictogram:
Signal Word:Warning
Hazard Statements:H302
Precautionary Statements:P280-P305+P351+P338

Related Pathways of Everolimus

PI3K-AKT

Isoform Comparison

Biological Activity

Target
  • mTOR

    mTOR (FKBP12), IC50:1.6 nM-2.4 nM

In Vitro:

Cell Line
Concentration Treated Time Description References
T47D 100 nM 6-12 months Generate Everolimus-resistant cell lines and confirm their resistance PMC10541180
MCF7 100 nM 6-12 months Generate Everolimus-resistant cell lines and confirm their resistance PMC10541180
CAMA-1 50 nM 6-12 months Generate Everolimus-resistant cell lines and confirm their resistance PMC10541180
LoVo cells 10 nM, 100 nM, 1 µM 72 h To evaluate the effects of Everolimus on cell cycle, cell death, and autophagy in LoVo cells. Results showed that Everolimus had minor effects on LoVo cells. PMC8531384
MDST8 cells 10 nM, 100 nM, 1 µM 72 h To evaluate the effects of Everolimus on cell cycle, cell death, and autophagy in MDST8 cells. Results showed that Everolimus significantly inhibited MDST8 cell growth, induced cell cycle arrest, and autophagy. PMC8531384

In Vivo:

Species
Animal Model
Administration Dosage Frequency Description References
Nude mice MDST8 tumor model Intraperitoneal injection 4 mg/kg Biweekly for 3 months To evaluate the therapeutic effects of Everolimus on MDST8 tumors. Results showed that Everolimus significantly reduced MDST8 tumor volume and extended the lifespan of mice. PMC8531384

Clinical Trial:

NCT Number Conditions Phases Recruitment Completion Date Locations
NCT01462214 Metastatic Renal Cell Cancer PHASE1|PHASE2 COMPLETED 2025-01-17 Medisch Centrum Alkmaar, Alkma... More >>ar, Netherlands|VU University Medical Center, Amsterdam, 1081 HV, Netherlands|NKI-AVL, Amsterdam, Netherlands|Haga Ziekenhuis, Den Haag, Netherlands|Medisch Centrum Haaglanden, Den Haag, Netherlands|Universitair Medisch Centrum Groningen, Groningen, Netherlands|Spaarne Ziekenhuis Hoofddorp, Hoofddorp, Netherlands|Medisch Centrum Leeuwarden, Leeuwarden, Netherlands|University Hospital Maastricht, Maastricht, Netherlands|St. Antonius Ziekenhuis, Nieuwegein, Netherlands|UMC St Radboud Nijmegen, Nijmegen, Netherlands|Sint Franciscus Gasthuis Rotterdam, Rotterdam, Netherlands|Isala Klinieken Zwolle, Zwolle, Netherlands Less <<
NCT00714025 Transitional Cell Carcinoma PHASE2 COMPLETED 2025-01-12 Cliniques Universitaires St Lu... More >>c-UCL, Bruxelles, 1200, Belgium Less <<
NCT01734512 Pediatric Recurrent Progressiv... More >>e Low-grade Gliomas|Pediatric Progressive Low-grade Gliomas Less << PHASE2 COMPLETED 2024-07-31 Children's Hospital Los Angele... More >>s, Los Angeles, California, 90027, United States|University of California, Los Angeles, Los Angeles, California, 90027, United States|Children's Hospital Oakland, Oakland, California, 94609, United States|University of California, San Diego Rady Children's Hospital, San Diego, California, 92123, United States|University of California, San Francisco, San Francisco, California, 94158, United States|Children's National Medical Center, Washington, District of Columbia, 20010, United States|University of Florida, Gainesville, Florida, 32611, United States|Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, 60611, United States|Johns Hopkins University, Baltimore, Maryland, 21218, United States|Dana-Farber Cancer Institute, Boston, Massachusetts, 02215, United States|Children's Hospitals and Clinics of Minneapolis, Minneapolis, Minnesota, 55404, United States|St. Louis Children's Hospital, Washington University, Saint Louis, Missouri, 63130, United States|Nationwide Children's Hospital, Columbus, Ohio, 43205, United States|Oregon Health & Science University, Portland, Oregon, 97239, United States|The Children's Hospital Of Philadelphia, Philadelphia, Pennsylvania, 19104, United States|St. Jude Children's Research Hospital, Memphis, Tennessee, 38105, United States|University of Utah, Salt Lake City, Utah, 84112, United States|University of Washington, Seattle, Seattle, Washington, 98195, United States Less <<
NCT02236572 Breast Cancer PHASE2 TERMINATED 2021-03-01 Yale University, New Haven, Co... More >>nnecticut, 06520, United States Less <<
NCT00457119 Non Small Cell Lung Cancer PHASE1 COMPLETED 2025-11-09 Georgetown University/Lombardi... More >> Cancer Center StudyCoordinator:CRAD001C2114, Washington, District of Columbia, 20007-2197, United States|LSU HEALTH SCIENCES CENTER/ LSU SCHOOL OF MEDICINE Feist-Weiller Cancer Center, New Orleans, Louisiana, 70115, United States|U of TX Southwestern Medical Center - SimmonsCompCancerCtr Clinical Research Office, Dallas, Texas, 75390-9151, United States|MD Anderson Cancer Center/University of Texas Thoractic Head/Neck Med. Onc., Houston, Texas, 77030-4009, United States|Novartis Investigative Site, Adelaide, South Australia, 5000, Australia|Novartis Investigative Site, Heidelberg, Victoria, 3084, Australia|Novartis Investigative Site, Essen, 45122, Germany|Novartis Investigative Site, Heidelberg, 69126, Germany Less <<
NCT01960829 Melanoma|TOR Serine-Threonine ... More >>Kinases|Neoplasm Metastasis Less << PHASE2 UNKNOWN - LuSi, Beijing, Beijing, 100142... More >>, China Less <<
NCT02352844 Solid Malignancy|Solid Tumor PHASE2 COMPLETED 2017-08-15 Washington University School o... More >>f Medicine, Saint Louis, Missouri, 63110, United States Less <<
NCT01663805 Delayed Function of Renal Tran... More >>splant Less << PHASE4 UNKNOWN 2025-06-15 Instituto de Urologia e Nefrol... More >>ogia, S?o José do Rio Preto, S?o Paulo, 15015-200, Brazil|Instituto de Urologia e Nefrologia, S?o José do Rio Preto, S?o Paulo, 15015-200, Brazil|Instituto de Urologia e Nefrologia, S?o José do Rio PReto, S?o Paulo, 15015200, Brazil Less <<
NCT00426049 Coronary Artery Disease|Corona... More >>ry Restenosis Less << PHASE3 UNKNOWN - German Heart Institute Berlin,... More >> Berlin, 13353, Germany Less <<
NCT00170885 Kidney Transplantation PHASE4 COMPLETED 2025-07-07 Novartis, Basel, Switzerland
NCT00811590 Peutz-Jeghers Syndrome PHASE2 TERMINATED 2025-03-11 Huntsman Cancer Institute, Sal... More >>t Lake City, Utah, 84112, United States Less <<
NCT01152840 Adenoid Cystic Carcinoma PHASE2 COMPLETED 2025-12-12 Seoul National University Hosp... More >>ital, Seoul, 110-744, Korea, Republic of Less <<
NCT00516165 Hepatocellular Carcinoma PHASE1|PHASE2 COMPLETED 2025-11-11 Massachusetts General Hospital... More >>, Boston, Massachusetts, 02114, United States|Dana-Farber Cancer Institute, Boston, Massachusetts, 02115, United States|Beth Israel Deaconess Medical Center, Boston, Massachusetts, 02215, United States Less <<
NCT00466466 Small-Cell Lung Cancer PHASE1 COMPLETED - Highlands Oncology Group, Faye... More >>tteville, Arkansas, 72703, United States|University of Colorado Health Sciences Center, Aurora, Colorado, 80045, United States|Dana Faber Cancer Institute, Boston, Massachusetts, 02115, United States|MD Anderson Cancer Center, Houston, Texas, 77030-4009, United States|Cancer Therapy and Research Center at UTHSCSA, San Antonio, Texas, 78229, United States|Novartis Investigative Site, Paris, France Less <<
NCT00098241 Kidney Transplantation PHASE3 COMPLETED 2025-03-07 Columbus Children's Hospital, ... More >>Columbus, Ohio, 43205-2696, United States|Dienst Pediatrie UZ Gasthuisberg, Herestraat 49, Leuven, 3000, Belgium Less <<
NCT00827359 Renal Cell Carcinoma|Renal Can... More >>cer Less << PHASE2 COMPLETED 2025-06-18 Beth Israel Deaconess Medical ... More >>Center, Boston, Massachusetts, 02215, United States|Dana-Farber Cancer Institute, Boston, Massachusetts, 02215, United States|Duke University Medical Center, Durham, North Carolina, 27710, United States Less <<
NCT01269684 Kidney Transplantation PHASE4 WITHDRAWN 2025-08-08 Novartis Investigative Site, Z... More >>urich, Switzerland Less <<
NCT01167530 Non-small Cell Lung Cancer|Loc... More >>ally Advanced Disease Less << PHASE1 UNKNOWN 2025-07-14 Institut Gustave Roussy, Ville... More >>juif, 94800, France Less <<
NCT00688623 Advanced and Metastatic Silent... More >> Neuro-Endocrine Tumors|Carcinoma|Neuroendocrine|Non Functioning Neuroendocrine Tumors (NETs)|Non Syndromic Neuroendocrine Tumors|Carcinoids|Non Functioning Less << PHASE2 COMPLETED 2016-11-07 Novartis Investigative Site, B... More >>ordeaux, France|Novartis Investigative Site, Lyon, France|Novartis Investigative Site, Marseille, France|Novartis Investigative Site, Paris, France|Novartis Investigative Site, Bad Berka, 99438, Germany|Novartis Investigative Site, Bad Berka, Germany|Novartis Investigative Site, Berlin, 13353, Germany|Novartis Investigative Site, Berlin, Germany|Novartis Investigative Site, Bonn, Germany|Novartis Investigative Site, Frankfurt, Germany|Novartis Investigative Site, Heidelberg, 69120, Germany|Novartis Investigative Site, Heidelberg, Germany|Novartis Investigative Site, Mainz, 55131, Germany|Novartis Investigative Site, Mainz, Germany|Novartis Investigative Site, Munich, Germany|Novartis Investigative Site, Bologna, BO, 40138, Italy|Novartis Investigative Site, Viagrande, CT, 95029, Italy|Novartis Investigative Site, Milano, MI, 20141, Italy|Novartis Investigative Site, Perugia, PG, 06129, Italy|Novartis Investigative Site, Roma, RM, 00189, Italy|Novartis Investigative Site, Bologna, Italy|Novartis Investigative Site, Milano, Italy|Novartis Investigative Site, Perugia, Italy|Novartis Investigative Site, Roma, Italy|Novartis Investigative Site, Viagrande, Italy|Novartis Investigative Site, Rotterdam, Netherlands|Novartis Investigative Site, Gdansk, 80-952, Poland|Novartis Investigative Site, Gdansk, Poland|Novartis Investigative Site, Warszawa, Poland|Novartis Investigative Site, Barcelona, Catalu?a, 08907, Spain|Novartis Investigative Site, Barcelona, Catalu?a, Spain|Novartis Investigative Site, Barcelona, Spain|Novartis Investigative Site, Madrid, Spain|Novartis Investigative Site, Uppsala, Spain|Novartis Investigative Site, Stockholm, Sweden|Novartis Investigative Site, Uppsala, SE-751 85, Sweden|Novartis Investigative Site, Glasgow - Scotland, G12 OYN, United Kingdom|Novartis Investigative Site, Glasgow, United Kingdom|Novartis Investigative Site, Manchester, M20 9BX, United Kingdom|Novartis Investigative Site, Manchester, United Kingdom Less <<
NCT02451696 Epilepsy|Tuberous Sclerosis Co... More >>mplex|Focal Cortical Dysplasia Less << PHASE2 COMPLETED 2017-12-28 New York University Langone Me... More >>dical Center, New York, New York, 10016, United States Less <<
NCT00170859 Heart Transplantation PHASE4 COMPLETED 2025-12-06 Novartis Investigational Site,... More >> Various Cities, Germany Less <<
NCT00655252 Metastatic Renal Cell Cancer NO_LONGER_AVAILABLE - Highlands oncology Group, PA, ... More >>Springdale, Arkansas, 72764, United States|University of Colorado Health Sciences Center/Anschutz Pavillion, Aurora, Colorado, 12801, United States|Cancer Centers of Florida, P.A., Ocoee, Florida, 34761, United States|MD Anderson Cancer Center - Orlando, Orlando, Florida, 32806, United States|Indiana University Cancer center, Indianapolis, Indiana, 46202, United States|The Cancer Institute, St. Joseph Medical Center, Towson, Maryland, 21209, United States|Henry Ford Health System, Detroit, Michigan, 48202, United States|Missouri Cancer Associates, Columbia, Missouri, 65201, United States|Heartland Hematology-Oncology Associates, Inc., Kansas City, Missouri, 64118, United States|Washington University/Siteman Cancer Center, St. Louis, Missouri, 63110, United States|Blumenthal Cancer Center/Carolinas Medical Center, Charlotte, North Carolina, 28203, United States|Gabrail Cancer Center, Canton, Ohio, 44718, United States|Cliveland Clinic Foundation, Cleveland, Ohio, 44195, United States|Cleo Craig Memorial Cancer & Research Clinic, Lawton, Oklahoma, 73505, United States|Cancer centers of the Carolinas, Greenville, South Carolina, 29615, United States|Novartis Investigative Site, Malvern, Australia|Novartis Investigative Site, Graz, Austria|Novartis Investigative Site, Linz, Austria|Novartis Investigative Site, Salzburg, Austria|Novartis Investigative Site, Vienna, Austria|Novartis Investigative Site, Brussels, Belgium|Moncton Hospital, Moncton, New Brunswick, E1C 6Z8, Canada|QE ll Health Sciences Centre, Halifax, Nova Scotia, B3H 2Y9, Canada|Royal Victoria Hospital, Barrie, Ontario, L4M 6M2, Canada|Lakeridhe Health Corp - Oshawa, Oshawa, Ontario, L1G 2B9, Canada|Sault Area Hospital - General Site, Sault Ste Marie, Ontario, P6A 2C4, Canada|Les Urologues Associes du CHUM, Montreal, Quebec, H2X 1N8, Canada|Centre Hospitalier Universitaire de Sherbrooke, Sherbrooke, Quebec, J1H 5N4, Canada|Saskatoon Cancer Center, Saskatoon, Saskatchewan, S7N 4H4, Canada|Novartis Investigative Site, Brno, Czech Republic|Novartis Investigative Site, Prague 2, Czech Republic|Novartis Investigative Site, Prague, Czech Republic|Novartis Investigative Site, Augsburg, Germany|Novartis Investigative Site, Bautzen, Germany|Novartis Investigative Site, Berlin, Germany|Novartis Investigative Site, Bremen, Germany|Novartis Investigative Site, Chemnitz, Germany|Novartis Investigative Site, Dresden, Germany|Novartis Investigative Site, Erlangen, Germany|Novartis Investigative Site, Essen, Germany|Novartis Investigative Site, Frankfurt/Main, Germany|Novartis Investigative Site, Frankfurt, Germany|Novartis Investigative Site, Freiburg, Germany|Novartis Investigative Site, Fulda, Germany|Novartis Investigative Site, Goslar, Germany|Novartis Investigative Site, Hamburg, Germany|Novartis Investigative Site, Hannover, Germany|Novartis Investigative Site, Jena, Germany|Novartis Investigative site, Koln, Germany|Novartis Investigative Site, Leipzig, Germany|Novartis Investigative Site, Magdeburg, Germany|Novartis Investigative Site, Mainz, Germany|Novartis Investigative Site, Mannheim, Germany|Novartis Investigative Site, Munchen, Germany|Novartis Investigative site, Munster, Germany|Novartis Investidative Site, Nurnberg, Germany|Novartis Investigative Site, Offenburg, Germany|Novartis Investigative Site, Oldenburg, Germany|Novartis Investigative Site, Recklinghausen, Germany|Novartis Investigative Site, Rostock, Germany|Novartis Investigative Site, Tubingen, Germany|Novartis Investigative Site, Wuppertal, Germany|Novartis Investigative Site, Budapest, Hungary|Novartis Investigative Site, Beirut, Lebanon|Novartis Investigative Site, Alesund, Norway|Novartis Investigative Site, Oslo, Norway|Novartis Investigative Site, Geneva, Switzerland|Novartis Investigative Site, St. Gallen, Switzerland|Novartis Investigative Site, Ankara, Turkey|Novartis Investigative Site, Istanbul, Turkey|Novartis Investigative Site, Izmir, Turkey|Royal Bournemouth Hospital, Bournemouth, BH7 7DW, United Kingdom|British Haematology and Oncology Centre, Bristol, BS2 8ED, United Kingdom|Addenbrookes Hospital, Cambridge, CB2 0QQ, United Kingdom|CRUK, Glasgow, G61 1BD, United Kingdom|Southampton University Hospital NHS Trust,, Hampshire, SO16 6YD, United Kingdom|Oncology & Haematology Clinical Tirals Unit, Leicester, LE1 5WW, United Kingdom|Royal Free Hospital, London, NW3 2QG, United Kingdom|Guy's and St. Thomas' NHS Foundation Trust, London, SE1 9RT, United Kingdom|Royal Marsden Hospital, London, SW3 6JJ, United Kingdom|The Christie Hospital, Manchester, M20 9BX, United Kingdom|Newcastle General Hospital, Newcastle, NE4 6BE, United Kingdom|Mount Vernon Cancer Centre, Northwood, HA6 2RN, United Kingdom|St Luke's Wing, Royal Surrey County Hospital, Surrey, GU2 7XX, United Kingdom|Singleton Hospital, Swansea, SA2 8QA, United Kingdom Less <<
NCT01609673 End Stage Renal Failure With R... More >>enal Transplant Less << TERMINATED 2025-05-13 Hospital S?o Jo?o de Deus/Fund... More >>a??o Geraldo Corrêa, Divinópolis, MG, 35500-227, Brazil|Hospital Márcio Cunha/Funda??o S?o Francisco Xavier, Ipatinga, MG, 35160-158, Brazil|Funda??o IMEPEN, Juiz de Fora, MG, 36036-330, Brazil|Hospital do Rim de MOntes Claros/Irmandade Nossa Senhora das Mercês, Montes Claros, MG, 39400-103, Brazil Less <<
NCT02338609 Growth and Development PHASE4 COMPLETED 2023-12-18 University Of California LA SC... More >>, Los Angeles, California, 90095, United States|Minnesota Epilepsy Group, Saint Paul, Minnesota, 55102, United States|Cinn Children Hosp Medical Center SC, Cincinnati, Ohio, 45229-3039, United States|Texas Scottish Rite Hos for Child SC, Dallas, Texas, 75219, United States|Novartis Investigative Site, Brussel, 1090, Belgium|Novartis Investigative Site, Moscow, 127412, Russian Federation Less <<
NCT03493165 Uterine Sarcoma AVAILABLE - -
NCT01059318 Lymphangioleiomyomatosis PHASE2 COMPLETED 2025-06-12 Center for LAM Research and Cl... More >>inical Care, Boston, Massachusetts, 02115, United States|University of Cincinnati, Department of Internal Medicine, Pulmonary, Critical Care & Sleep Medicine,, Cincinnati, Ohio, 45267, United States|Novartis Investigative Site, Lyon, France|Novartis Investigative Site, Milan, Italy Less <<
NCT01482299 Stomach Neoplasm PHASE2 COMPLETED 2025-01-14 Asan Medical Center, Songpa-gu... More >>, Seoul, Korea, Republic of Less <<
NCT01491672 Metastatic Renal Cell Carcinom... More >>a Less << PHASE2 COMPLETED 2025-05-15 Memorial Sloan Kettering Cance... More >>r Center, NY, New York, 90033, United States|Novartis Investigative Site, Rio Negro, Viedma, 8500, Argentina|Novartis Investigative Site, Tucuman, T4000, Argentina|Novartis Investigative Site, Florianopolis, SC, 88034-000, Brazil|Novartis Investigative Site, Barretos, SP, 14784-400, Brazil|Novartis Investigative Site, S?o Paulo, SP, 01246-000, Brazil|Novartis Investigative Site, S?o Paulo, SP, 01509-900, Brazil|Novartis Investigative Site, Sofia, 1784, Bulgaria|Novartis Investigative Site, Beijing, Beijing, 100730, China|Novartis Investigative Site, Hangzhou, Zhejiang, 310003, China|Novartis Investigative Site, Beijing, 100021, China|Novartis Investigative Site, Guangzhou, 510060, China|Novartis Investigative Site, Shanghai, 200032, China|Novartis Investigative Site, Leningrad Region, Russia, 188663, Russian Federation|Novartis Investigative Site, Moscow, Russia, 125284, Russian Federation|Novartis Investigative Site, Nizhny Novgorod, Russia, 603001, Russian Federation|Novartis Investigative Site, Obninsk, Russia, 249036, Russian Federation Less <<
NCT01509560 Condition After Allogenic Peri... More >>pheral Stem Cell Transplantation (SCT) Less << PHASE2 COMPLETED 2016-04-30 Zentrum für Knochenmark- und B... More >>lutstammzelltransplantation,, Wiesbaden, Hessen, 65191, Germany Less <<
NCT01566279 Unspecified Adult Solid Tumor,... More >> Protocol Specific Less << COMPLETED 2025-11-16 NKI-AVL, Amsterdam, Noord Holl... More >>and, 1066 CX, Netherlands|Erasmus Medical Center, Rotterdam, Zuid Holland, 3075 EA, Netherlands|University Medical Center Utrecht, Utrecht, 3584 CX, Netherlands Less <<
NCT00446368 Carcinoma, Renal Cell PHASE2 COMPLETED 2025-10-08 Baylor College of Medicine - M... More >>ethodist Hospital, Houston, Texas, 77030, United States Less <<
NCT02809404 Breast Cancer|Renal Cell Carci... More >>noma Less << COMPLETED 2025-01-17 Radboud university medical cen... More >>ter, Nijmegen, Netherlands Less <<
NCT01216839 Refractory or Relapsed RMS and... More >> Soft Tissue Sarcomas Less << PHASE2 UNKNOWN 2025-12-13 Casa de Saúde Santa Marcelina,... More >> Sao Paulo, SP, 08270070, Brazil Less <<
NCT01637090 Cutaneous T-Cell Lymphoma PHASE2 TERMINATED 2025-05-15 Boston Medical Center, Boston,... More >> Massachusetts, 02118, United States Less <<
NCT00702052 Lymphoma, Mantle- Cell PHASE2 COMPLETED 2012-04-20 Mayo Clinic - Arizona Mayo Cli... More >>nic - Scottsdale, Multiple Locations, Arizona, 85259, United States|Highlands Oncology Group DeptofHighlandsOncologyGrp(2), Fayetteville, Arkansas, 72703, United States|Bay Area Cancer Research Dept.ofBayAreaCancerResearch, Concord, California, 94520, United States|City of Hope National Medical Center Dept.ofCityofHopeMedicalCtr(1), Duarte, California, 91010-3000, United States|UCLA/ University of California Los Angeles Dept.of Hem/Oncology, Los Angeles, California, 90095, United States|University of California Davis Cancer Center Dept. of UC Davis Cancer (4), Sacramento, California, 95817, United States|Rocky Mountain Cancer Centers RMCC - Denver-Midtown, Greenwood Village, Colorado, 80121, United States|Advanced Medical Specialties Medical Onc Hem, Miami, Florida, 33176, United States|Georgia Health Sciences University Dept. of MCG, Augusta, Georgia, 30912, United States|Northwestern University, Chicago, Illinois, 60611, United States|St. Francis Cancer Research Foundation Dept.ofSt.FrancisCancerRes.(2), Beech Grove, Indiana, 46107, United States|Central Indiana Cancer Centers CICC - East (2), Indianapolis, Indiana, 46227, United States|University of Michigan Comprehensive Cancer Center Dept of Michigan Cancer Center, Ann Arbor, Michigan, 48109-0944, United States|Mayo Clinic - Rochester Hematology, Rochester, Minnesota, 55905, United States|Washington University School Of Medicine-Siteman Cancer Ctr Medical Oncology, Saint Louis, Missouri, 63110, United States|Hackensack University Medical Center Dept ofHackensackUniversityMC, Hackensack, New Jersey, 07601, United States|New York University Medical Center NYU Cancer Institute, New York, New York, 10016, United States|East Carolina University BrodySchool of Medicine, Greenville, North Carolina, 27858, United States|Northwest Cancer Specialists Vancouver Cancer Center (2), Portland, Oregon, 97210, United States|Kaiser Permanente Northwest Dept of Kaiser Northwest (3), Portland, Oregon, 97227, United States|Fox Chase Cancer Center Regulatory Contact, Philadelphia, Pennsylvania, 19111-2497, United States|Western Pennsylvania Cancer Institute /Western Penn Hospital Western Pann. Cancer Inst., Pittsburgh, Pennsylvania, 15224, United States|University of Pittsburgh Medical Center Hillman Cancer Center (4), Pittsburgh, Pennsylvania, 15232, United States|Cancer Centers of the Carolinas CC of C -Eastside, Greenville, South Carolina, 29605, United States|Vanderbilt University Medical Center, Clinical Trials Center Dept. of VUMC, Nashville, Tennessee, 37212, United States|Baylor College of Medicine Dept. of Sammons Cancer (2), Dallas, Texas, 75246, United States|University of Texas Southwestern Medical Center DeptofSimmons Cancer Center(2), Dallas, Texas, 75390-8527, United States|MD Anderson Cancer Center/University of Texas Dept. of MD Anderson (10), Houston, Texas, 77030-4009, United States|Tyler Cancer Center Dept.ofTylerCancerCtr., Tyler, Texas, 75702, United States|Cancer Care Northwest CC Northwest- Spokane South(3), Spokane, Washington, 99202, United States|West Virginia University/ Mary Babb Randolph Cancer Center, Morgantown, West Virginia, 26506, United States Less <<
NCT00401778 Lung Cancer PHASE1 COMPLETED 2025-12-13 Emory University Winship Cance... More >>r Institute, Atlanta, Georgia, 30322, United States Less <<
NCT00529802 Carcinoma, Renal Cell PHASE2 COMPLETED 2025-07-10 University of Chicago, Chicago... More >>, Illinois, 60637, United States|Oncology/Hematology Associates, Peoria, Illinois, 61615, United States|Beth Israel Deaconess Med Ctr, Boston, Massachusetts, 02215, United States|Washington University, Saint Louis, Missouri, 63110, United States|The University of North Carolina at Chapel Hill, Lineberger Comprehensive Cancer Center, Chapel Hill, North Carolina, 27599, United States Less <<
NCT01239472 Renal Transplant Rejection|Imm... More >>unosuppression Less << PHASE4 COMPLETED 2025-06-15 Santa Casa de Misericórdia de ... More >>Belo Horizonte, Belo Horizonte, Minas Gerais, 30150221, Brazil Less <<
NCT02332902 Neurofibromatosis 1 PHASE2 COMPLETED 2025-03-16 The University of Texas Health... More >> Science Center at Houston, Houston, Texas, 77030, United States Less <<
NCT01514110 Gastric Cancer PHASE1|PHASE2 COMPLETED 2019-03-06 Department of Clinical Oncolog... More >>y, Prince of Wales Hospital, Hong Kong, Hong Kong Less <<
NCT00629525 Hormone Refractory Prostate Ca... More >>ncer Less << PHASE2 COMPLETED 2025-01-10 Duke University MEdical Center... More >>, Durham, North Carolina, 27710, United States Less <<
NCT00976248 Waldenstrom's Macroglobulinemi... More >>a Less << PHASE2 COMPLETED 2025-07-18 Dana-Farber Cancer Institute, ... More >>Boston, Massachusetts, 02115, United States Less <<
NCT01653041 Kidney Transplantation PHASE4 COMPLETED 2025-04-15 Hospital do Rim e Hipertens?o,... More >> S?o Paulo, 04038-002, Brazil Less <<
NCT01216826 Refractory or Relapsed Osteosa... More >>rcoma Less << PHASE2 UNKNOWN 2025-12-14 Hospital Santa Marcelina, Sao ... More >>Paulo, SP, 08270070, Brazil Less <<
NCT00087685 Endometrial Cancer PHASE2 COMPLETED 2025-01-15 University of Texas MD Anderso... More >>n Cancer Center, Houston, Texas, 77030, United States Less <<
NCT01830153 Soft Tissue Sarcomas|Bone Sarc... More >>omas Less << PHASE2 COMPLETED - Seoul National University Bund... More >>ang Hospital, Seongnam, Gyeonggi, 463-707, Korea, Republic of|Asan Medical Center, University of Ulsan College of Medicine, Seoul, N/A = Not Applicable, 138-736, Korea, Republic of|Yeongnam University College of Medicine, Daegu, Korea, Republic of|Chungnam National University Hospital, Daejeon, 301-721, Korea, Republic of|Seoul National University Hospital, Seoul, 110-744, Korea, Republic of|Yonsei Cancer Center, Seoul, 120-752, Korea, Republic of|Korea University, Seoul, 126-1, Korea, Republic of|Samsung Medical Center, Seoul, 135-710, Korea, Republic of Less <<
NCT00150046 Heart Transplantation PHASE3 COMPLETED - Novartis Investigational Site,... More >> Germany, Germany|Basel Novartis Pharma AG, Basel, Switzerland Less <<
NCT01594268 Kidney Transplant PHASE4 COMPLETED 2025-10-13 Novartis Investigative Site, S... More >>eoul, Korea, 120-752, Korea, Republic of|Novartis Investigative Site, Seoul, 135-720, Korea, Republic of|Novartis Investigative Site, Seoul, 738-736, Korea, Republic of|Novartis Investigative Site, Suwon, 442-721, Korea, Republic of Less <<
NCT01070316 Epilepsy|Tuberous Sclerosis Co... More >>mplex Less << PHASE1|PHASE2 COMPLETED 2025-04-16 Cincinnati Children's Hospital... More >> Medical Center, Cincinnati, Ohio, 45229, United States|Baylor College of Medicine, Houston, Texas, 77030, United States Less <<
NCT00505102 Kidney Diseases|Heart Transpla... More >>ntation Less << PHASE4 UNKNOWN 2025-07-09 Heart Transplant Center Ospeda... More >>li Riuniti, Bergamo, 24100, Italy|Heart Transplantad Center OspedaliRiuniti Bergamo, Bergamo, 24100, Italy Less <<
NCT00805129 Bladder Cancer|Metastatic Tran... More >>sitional Cell Carcinoma Less << PHASE2 COMPLETED 2021-12-15 Memorial Sloan Kettering Cance... More >>r Center, New York, New York, 10065, United States Less <<
NCT02017860 Neoplasms PHASE2 COMPLETED 2019-04-25 Novartis Investigative Site, M... More >>atsuyama, Ehime, 791-0280, Japan|Novartis Investigative Site, Sapporo city, Hokkaido, 060 8648, Japan|Novartis Investigative Site, Osaka-city, Osaka, 540-0006, Japan|Novartis Investigative Site, Kitaadachi-gun, Saitama, 362-0806, Japan Less <<
NCT00936858 Thyroid Cancer PHASE2 COMPLETED 2020-02-27 Massachusetts General Hospital... More >>, Boston, Massachusetts, 02114, United States|Dana-Farber Cancer Institute, Boston, Massachusetts, 02115, United States|Mt. Sinai Medical Center, New York, New York, 10029, United States|MD Anderson Cancer Center, Houston, Texas, 77030, United States Less <<
NCT00170833 Renal Transplantation PHASE3 COMPLETED - -
NCT00729482 Stomach Neoplasm PHASE2 COMPLETED 2025-03-13 Asan Medical Center, Seoul, So... More >>ngpa, 138-736, Korea, Republic of Less <<
NCT01888042 Kidney Cancer PHASE2 TERMINATED 2025-07-14 Gustave Roussy, Villejuif, Val... More >> de Marne, 94805, France Less <<
NCT00968591 Hepatic Insufficiency PHASE1 COMPLETED - Novartis Investigative Site, F... More >>rankfurt, Germany|Novartis Investigative Site, Moscow, Russian Federation|Novartis Investigative Site, Singapore, Singapore Less <<
NCT00411619 Tuberous Sclerosis|Subependyma... More >>l Giant Cell Astrocytoma Less << PHASE1|PHASE2 COMPLETED 2025-01-14 Cincinnati Children's Hospital... More >> Medical Center, Cincinnati, Ohio, 45229, United States Less <<
NCT02504892 Renal Cancer|Birt-Hogg-Dube Sy... More >>ndrome Less << PHASE2 TERMINATED 2018-04-17 National Institutes of Health ... More >>Clinical Center, 9000 Rockville Pike, Bethesda, Maryland, 20892, United States Less <<
NCT01152827 Pheochromocytoma|Extra-adrenal... More >> Paraganglioma|Non-functioning Carcinoid Less << PHASE2 COMPLETED 2025-12-11 Seoul National University Hosp... More >>ital, Seoul, 110-744, Korea, Republic of Less <<
NCT00799188 Cardiac Transplantation|Skin C... More >>ancer Less << PHASE3 UNKNOWN - HOSPICES CIVILS de LYON, Lyon,... More >> France Less <<
NCT00337545 Colorectal Cancer PHASE2 COMPLETED 2025-04-07 Swedish Cancer Institute, Seat... More >>tle, Washington, 98104, United States Less <<
NCT03955172 Kidney Transplant Failure and ... More >>Rejection Less << RECRUITING 2027-12-03 Service de transplantation, né... More >>phrologie et immunologie clinique, H?pital Edouard Herriot (HCL), Lyon, 69003, France Less <<
NCT00830895 Renal Cell Carcinoma PHASE2 COMPLETED 2025-12-12 Seoul National University Hosp... More >>ital, Seoul, Korea, Republic of Less <<
NCT02201212 TSC1|TSC2|Tuberous Sclerosis C... More >>omplex|MTOR Less << PHASE2 COMPLETED 2025-06-19 Dana Farber Cancer Institute, ... More >>Boston, Massachusetts, 02115, United States|Memorial Sloan Kettering Cancer Center, New York, New York, 10065, United States Less <<
NCT01525719 Cholangiocarcinoma PHASE2 UNKNOWN 2025-06-14 -
NCT02056587 Metastatic Renal Cell Carcinom... More >>a Less << PHASE4 COMPLETED 2025-10-13 Tatarstan Regional Cancer Cent... More >>er, Kazan, Tatarstan, 420029, Russian Federation|Altai Regional Cancer Center, Barnaul, Russian Federation|N.N. Blokhin Russian Cancer Research Center, Moscow, 115478, Russian Federation Less <<
NCT02569125 Segmental Overgrowth Syndrome PHASE2 WITHDRAWN 2025-02-16 Vivantes Klinikum Neuk?lln, Be... More >>rlin, 12351, Germany|Universit?tsklinikum Bonn, Bonn, 53113, Germany|Universit?tsklinikum Freiburg, Freiburg, 79106, Germany|Universit?tsklinikum Leipzig, Leipzig, 04103, Germany Less <<
NCT02273752 Estrogen Receptor-positive Bre... More >>ast Cancer|Gastrinoma|Glucagonoma|HER2-negative Breast Cancer|Insulinoma|Mucositis|Oral Complications|Pancreatic Polypeptide Tumor|Progesterone Receptor-positive Breast Cancer|Recurrent Breast Cancer|Recurrent Islet Cell Carcinoma|Recurrent Renal Cell Cancer|Somatostatinoma|Stage III Renal Cell Cancer|Stage IIIA Breast Cancer|Stage IIIB Breast Cancer|Stage IIIC Breast Cancer|Stage IV Breast Cancer|Stage IV Renal Cell Cancer Less << PHASE2 TERMINATED 2025-12-15 Emory University Hospital Midt... More >>own, Atlanta, Georgia, 30308, United States|Emory University/Winship Cancer Institute, Atlanta, Georgia, 30322, United States Less <<
NCT04867720 Liver Transplant PHASE4 UNKNOWN 2023-02-22 Seoul National University Hosi... More >>pital, Seoul, Korea, Republic of Less <<
NCT03493152 Gastrointestinal Stromal Tumor TEMPORARILY_NOT_AVAILABLE - -
NCT01648465 Gastrointestinal Tumors|Pancre... More >>atic Tumors|Gastrointestinal Neuroendocrine Tumors|Pancreatic Neuroendocrine Tumors Less << PHASE2 TERMINATED 2019-08-06 2nd Dept of Internal Medicine,... More >> Agios Savvas Cancer Hospital, Athens, 11522, Greece|Dept of Medical Oncology, 251 General Airforce Hospital, Athens, 11525, Greece|2nd Dept of Internal Medicine, General Hospital of Athens "Hippokratio", Athens, 11527, Greece|2nd Dept of Internal Medicine, Propaedeutic, University Hospital "Attikon", Athens, 12462, Greece|4th Dept of Internal Medicine, University Hospital "Attiko", Athens, 12462, Greece|3rd Dept of Medical Oncology, Agii Anargiri Cancer Hospital, Athens, 14564, Greece|2nd Dept of Medical Oncology, Metropolitan Hospital, Athens, 18547, Greece|Dept of Medical Oncology, University Hospital of Heraklion, Heraklion, 71110, Greece|Dept of Medical Oncology, Ioannina University Hospital, Ioannina, 45110, Greece|Division of Oncology, Dept of Internal Medicine, University Hospital of Patras, Patra, 26504, Greece|Dept of Medical Oncology, Papageorgiou General Hospital, Thessaloniki, 56429, Greece|Dept of Medical Oncology, Thermi Clinic, Thessaloniki, 57001, Greece Less <<
NCT01088893 Breast Neoplasms PHASE2 UNKNOWN 2025-03-13 Unimed Medical Institute, Hong... More >> Kong, China Less <<
NCT01561404 Disorder Related to Renal Tran... More >>splantation|Exercise, Aerobic|Muscle Strength Less << PHASE4 TERMINATED 2025-12-13 Nephrology Department. Hospita... More >>l Universitari de Bellvitge, L'Hospitalet de Llobregat, Barcelone, 08907, Spain Less <<
NCT01636466 Kidney Failure, Chronic PHASE3 TERMINATED 2025-05-14 Emory University, Atlanta, Geo... More >>rgia, 30322, United States Less <<
NCT01164267 Marginal Zone B-cell Lymphoma PHASE2 COMPLETED - General Hospital AKH, Vienna, ... More >>Austria|Policlinico S. Orsola Malpighi, Bologna, Italy|IEO, Milano, Italy|INT, Milano, Italy|Humanitas, Milan, Italy|San Raffaele Hospital, Milan, Italy|AOU Maggiore della Carità, Novara, Italy|IRCCS Policlinico S. Matteo, Pavia, Italy|AOU S. Giovanni Battista, Torino, Italy|IOSI, Bellinzona, Switzerland Less <<
NCT01009957 Polycystic Kidney Diseases PHASE2|PHASE3 TERMINATED 2025-06-15 A.O. Spedali Civili Di Brescia... More >>, Brescia, Italy|Alessandro Manzoni Hospital, Nephrology and Dialysis Department, Lecco, 23900, Italy|Modena Hospital, Modena, 41100, Italy|Dipartimento di Patologia Sistematica - Università Federico 2°, Napoli, 80138, Italy|Ospedale "Guglielmo da Saliceto" - Nephrology and Dialysis Department, Piacenza, 29100, Italy|C.M.I.D. - Presidi Ospedalieri ASL 4, Torino, 10152, Italy|Ospedale Civile San Bortolo Vicenza, Vicenza, Italy Less <<
NCT03629847 Neuroendocrine Tumors PHASE1|PHASE2 UNKNOWN 2025-12-18 Oncology Centre, King Faisal S... More >>pecialist Hospital & Research Center, Riyadh, 11211, Saudi Arabia Less <<
NCT00187174 Tumors|Brain Tumors|Rhabdomyos... More >>arcoma|Sarcoma, Soft Tissue Less << PHASE1 COMPLETED 2025-10-08 St. Jude Children's Research H... More >>ospital, Memphis, Tennessee, 38105, United States Less <<
NCT01399242 Disorder Related to Renal Tran... More >>splantation Less << PHASE4 UNKNOWN 2025-06-13 Hospital Universitário S?o Jos... More >>é, Belo Horizonte, Minas Gerais, 30140-073, Brazil Less <<
NCT02493465 Left Ventricular Hypertrophy PHASE4 UNKNOWN 2025-07-17 Instituto de Urologia e Nefrol... More >>ogia, S?o José do Rio Preto, S?o Paulo, 15015-200, Brazil Less <<
NCT02049047 Thymoma and Thymic Carcinoma PHASE2 COMPLETED 2025-01-19 Istituto Clinico Humanitas, Ro... More >>zzano, MI, 20089, Italy Less <<
NCT01423708 Liver Failure|Liver Diseases|L... More >>iver Cirrhosis|Liver Neoplasms Less << PHASE2 UNKNOWN 2025-01-14 Ospedali Riuniti - Bergamo, Be... More >>rgamo, BG, 24128, Italy|Irccs Ospedale Maggiore Policlinico Di Milano, Milano, MI, 20122, Italy|Ospedale Ca' Granda-Niguarda - Milano, Milano, MI, 20162, Italy|Azienda Ospedaliera di Padova, Padua, PD, 35128, Italy|Policlinico Universitario Gemelli Di Roma, Roma, RM, 00168, Italy|A.O. Universitaria S. Giovanni Battista-Molinette Di Torino, Torino, TO, 10126, Italy|A.O. Universitaria S. Maria Della Misericordia Di Udine, Udine, UD, 33100, Italy Less <<
NCT01266837 Metastatic Renal Cell Carcinom... More >>a|Failure of Exactly One Prior VEGF-targeted Therapy Less << PHASE4 COMPLETED 2017-10-31 Charitè Campus Benjamin Frankl... More >>in, Berlin, 12203, Germany|Klinik und Poliklinik für Urologie , Universit?tsklinikum Carl Gustav Carus der Technischen Universit?t Dresden, Dresden, 01307, Germany|Urologie - Waldkrankenhaus St. Marien, Erlangen, 91054, Germany|Klinik für Innere Medizin (Tumorforschung), Universit?tsklinikum Essen, Essen, 45122, Germany|Zentrum Innere Medizin, Medizinische Hochschule Hannover, Hannover, 30625, Germany|Klinik für Urologie und Kinderurologie, Universit?tsklinikum des Saarlandes, Homburg, 66421, Germany|Klinik für Urologie, Universit?tsklinikum Jena, Jena, 07743, Germany|5. Medizinische Klinik, Klinikum Nürnberg, Nürnberg, 90419, Germany Less <<
NCT01466231 Germ Cell Tumor PHASE2 COMPLETED 2025-06-15 National Cancer Institute, Bra... More >>tislava, 83310, Slovakia Less <<
NCT00409292 Pancreatic Cancer PHASE2 COMPLETED 2025-05-09 Massachusetts General Hospital... More >>, Boston, Massachusetts, 02114, United States|Beth Israel Deaconess Medical Center, Boston, Massachusetts, 02115, United States|Dana-Farber Cancer Institute, Boston, Massachusetts, 02115, United States Less <<
NCT00657982 Prostate Cancer PHASE2 UNKNOWN - Sheba Medical Center, Tel Hash... More >>omer, 52621, Israel Less <<
NCT02155920 Recurrent Childhood Ependymoma PHASE2 COMPLETED 2023-07-14 Lucile Packard Children's Hosp... More >>ital Stanford University, Stanford, California, 94305, United States|New York University Stephen D. Hassenfeld Children's Center for Cancer & Blood Disorders, New York, New York, 10016, United States|UT Southwestern Medical Center / Children's Medical Center, Dallas, Texas, 75390, United States|Baylor College of Medicine / Texas Children's Hospital, Houston, Texas, 77030, United States Less <<
NCT02338570 Renal Cell Carcinoma PHASE4 TERMINATED 2025-02-18 Spedali Civili, Brescia, Italy... More >>|Ospedale A Perrino, Brindisi, Italy|Istituto Europeo di Oncologia, Milano, Italy|Istituto Nazionale Tumori - IRCCS Fondazione G. Pascale, Napoli, Italy|AOU Maggiore della Carità, Novara, Italy|Casa di Cura La Maddalena, Palermo, Italy|Unicampus Biomedico, Roma, Italy|AOU San Giovanni di Dio e Ruggi D'Aragona, Salerno, Italy Less <<
NCT01048723 Sarcoma PHASE2 TERMINATED 2025-10-11 H. Lee Moffitt Cancer Center a... More >>nd Research Institute, Tampa, Florida, 33612, United States Less <<
NCT02687958 Neuroendocrine Carcinoma PHASE2 ACTIVE_NOT_RECRUITING 2025-12-23 S.C. Oncologia - Policlinico, ... More >>Modena, Emilia - Romagna, 41124, Italy|U.O. Oncologia Medica 1 - AOU Pisana, Pisa, Tuscany, 56126, Italy|Azienda Ospedaliera "Spedali Civili di Brescia", Brescia, 25123, Italy|Azienda Ospedaliera Universitaria Careggi, Florence, 50134, Italy|Istituto Europeo di Oncologia, Milano, 20141, Italy Less <<
NCT01997255 Sturge Weber Syndrome PHASE2 WITHDRAWN 2025-04-16 Texas Children's Hospital, Hou... More >>ston, Texas, 77030, United States Less <<
NCT01324492 Lung Neuroendocrine Neoplasm PHASE1 COMPLETED 2025-06-14 Novartis Investigative Site, B... More >>eijing, Beijing, 100730, China|Novartis Investigative Site, Guangzhou, Guangdong, 510030, China|Novartis Investigative Site, Changchun, Jilin, China|Novartis Investigative Site, Shenyang, Liaoning, China Less <<
NCT00124280 Non-small-cell Lung Carcinoma PHASE2 COMPLETED - Nevada Cancer Institute, Las V... More >>egas, Nevada, 89135, United States|MD Anderson Cancer Center, Department of Thoracic /Head and Neck Medical Oncology, Houston, Texas, 77030, United States Less <<
NCT00081874 Leukemia|Mantle Cell Lymphoma|... More >>Myelofibrosis Less << PHASE1|PHASE2 COMPLETED 2025-09-06 M.D. Anderson Cancer Center, H... More >>ouston, Texas, 77030, United States Less <<
NCT00767819 Progressive Sarcoma PHASE2 COMPLETED 2017-05-17 Novartis Investigative Site, B... More >>ad Saarow, 15526, Germany|Novartis Investigative Site, Duesseldorf, 40479, Germany|Novartis Investigative Site, Essen, 45147, Germany|Novartis Investigative Site, Mannheim, 68167, Germany|Novartis Investigative Site, Muenchen, 81377, Germany|Novartis Investigative Site, Milano, MI, 20133, Italy Less <<
NCT02205515 Carcinoma, Neuroendocrine PHASE1|PHASE2 COMPLETED 2025-10-21 Odette Cancer Centre, Sunnybro... More >>ok Health Science Centre, Toronto, Ontario, M4N 3M5, Canada Less <<
NCT00373815 Graft Versus Host Disease PHASE1 TERMINATED 2025-10-09 Medical Center, Hematology & O... More >>ncology, University of Tuebingen, Tuebingen, D-72076, Germany Less <<
NCT01206764 Renal Cell Carcinoma PHASE4 COMPLETED 2017-07-01 Novartis Investigative Site, A... More >>lger, 016000, Algeria|Novartis Investigative Site, Oran, Algeria|Novartis Investigative Site, Alexandria, 21131, Egypt|Novartis Investigative Site, Cairo, Egypt|Novartis Investigative Site, Mansoura, Egypt|Novartis Investigative Site, Indore, Madhya Pradesh, 452 008, India|Novartis Investigative Site, Pune, Maharashtra, 411013, India|Novartis Investigative Site, Amman, 11941, Jordan|Novartis Investigative Site, Ashrafieh, 166830, Lebanon|Novartis Investigative Site, Moscow, 115478, Russian Federation|Novartis Investigative Site, Samara, 443031, Russian Federation|Novartis Investigative Site, Riyadh, 11211, Saudi Arabia|Novartis Investigative Site, Cape Town, 7500, South Africa|Novartis Investigative Site, Cape Town, 7925, South Africa|Novartis Investigative Site, Durban, 4001, South Africa|Novartis Investigative Site, Parktown, 2193, South Africa|Novartis Investigative Site, Songkhla, Hat Yai, 90110, Thailand|Novartis Investigative Site, Bangkok, 10400, Thailand|Novartis Investigative Site, Chiang Mai, 50200, Thailand|Novartis Investigative Site, Tunis, Tunisie, 1007, Tunisia|Novartis Investigative Site, Ariana, 2080, Tunisia|Novartis Investigative Site, Sousse, 4000, Tunisia Less <<
NCT02539459 Sporadic Angiomyolipomas (AMLs... More >>) Less << PHASE2 TERMINATED 2018-08-20 Yale School of Medicine, New H... More >>aven, Connecticut, United States|Dana Farber Cancer Institute, Boston, Massachusetts, United States|Mayo Clinic, Rochester, Minnesota, United States|Memorial Sloan Kettering, New York, New York, United States|Duke University Health System, Durham, North Carolina, United States|Fox Chase Cancer Center, Philadelphia, Pennsylvania, 19111, United States|University of Pennsylvania, Philadelphia, Pennsylvania, United States|M D Anderson Cancer Center, Houston, Texas, United States Less <<
NCT00688753 Carcinoma|Renal Cell|Non Clear... More >> Cell Renal Carcinoma|Papillary Cell Renal Carcinoma|Adenocarcinoma Less << PHASE2 COMPLETED 2025-10-14 Novartis Investigative Site, B... More >>russels, BE-B-1200, Belgium|Novartis Investigative Site, Gent, 9000, Belgium|Novartis Investigative Site, Bordeaux Cedex, 33075, France|Novartis Investigative Site, Lyon Cedex, 69373, France|Novartis Investigative Site, Marseille, 13273, France|Novartis Investigative Site, Paris, 75015, France|Novartis Investigative Site, Villejuif Cedex, 94805, France|Novartis Investigative Site, Berlin, 10098, Germany|Novartis Investigative Site, Hannover, 30625, Germany|Novartis Investigative Site, Muenster, 48149, Germany|Novartis Investigative Site, Arezzo, AR, 52100, Italy|Novartis Investigative Site, Cremona, CR, 26100, Italy|Novartis Investigative Site, Pavia, PV, 27100, Italy|Novartis Investigative Site, Napoli, 80132, Italy|Novartis Investigative Site, Otwock, 05-400, Poland|Novartis Investigative Site, Barcelona, Catalunya, 08003, Spain|Novartis Investigative Site, Barcelona, Catalu?a, 08907, Spain|Novartis Investigative Site, Valencia, Comunidad Valenciana, 46009, Spain|Novartis Investigative Site, Barcelona, 08041, Spain Less <<
NCT01490476 Neurofibromatosis 2 PHASE2 COMPLETED 2025-01-17 H?pital Beaujon, 100 boulevard... More >> du Général Leclerc, Clichy, 92110, France Less <<
NCT00519324 Advanced Gastric Cancer PHASE2 COMPLETED - Novartis investigative Site, A... More >>ichi, Japan|Novartis investigative Site, Chiba, Japan|Novartis investigative Site, Ehime, Japan|Novartis Investigative Site, Hokkaido, Japan|Novartis investigative Site, Osaka, Japan|Novartis investigative Site, Shizuoka, Japan|Novartis Investigative Site, Tochigi, Japan|Novartis investigative Site, Tokyo, Japan Less <<
NCT01880749 Neurofibromatosis Type 2|Vesti... More >>bular Schwannomas|Meningiomas Less << EARLY_PHASE1 COMPLETED 2025-12-19 New York University School of ... More >>Medicine, New York, New York, 10016, United States Less <<
NCT03525834 Renal Angiomyolipoma PHASE4 COMPLETED 2020-09-25 Novartis Investigative Site, W... More >>uhan, Hubei, 430030, China|Novartis Investigative Site, Shanghai, Shanghai, 200032, China|Novartis Investigative Site, Chengdu, Sichuan, 610041, China|Novartis Investigative Site, Beijing, 100028, China|Novartis Investigative Site, Beijing, 100730, China Less <<
NCT01178151 Peutz-Jeghers Syndrome|Neoplas... More >>tic Processes|Neoplasm Metastasis Less << PHASE2 WITHDRAWN 2025-04-15 Academic Medical Center, Amste... More >>rdam, 1105AZ, Netherlands|Erasmus Medical Center, Rotterdam, 3000 CA, Netherlands Less <<
NCT02812940 Graft-versus-Host Disease PHASE2 COMPLETED 2025-12-20 University of Cologne, Cologne... More >>, 50924, Germany Less <<
NCT00457964 Tuberous Sclerosis|Lymphangiol... More >>eiomyomatosis Less << PHASE1|PHASE2 COMPLETED 2025-07-13 Cincinnati Children's Hospital... More >> Medical Center, Cincinnati, Ohio, 45229, United States Less <<
NCT01631058 Chronic Renal Failure (CRF)|Gr... More >>aft Failure|Transplant; Failure, Kidney|Renal Transplant Rejection Less << PHASE4 UNKNOWN 2025-06-19 Clinical Hospital of the Schoo... More >>l of Medicine, University of Sao Paulo, Sao Paulo, SP, 05403900, Brazil|Clinical Hospital of the School of Medicine, University of Sao Paulo, Sao Paulo, SP, 05403900, Brazil Less <<
NCT00170820 Renal Transplantation PHASE4 COMPLETED - Novartis, Basel, Switzerland
NCT01715935 Clear-cell Renal Carcinoma|Cle... More >>ar-cell Metastatic Renal Cell Carcinoma Less << PHASE2 COMPLETED 2025-04-16 CHRU Besan?on, Besan?on, 25000... More >>, France|H?pital Henri Mondor, Créteil, 94000, France|Centre Hospitalier Départemental Vendée, La Roche-sur-Yon, 85925 cedex 9, France|H?pital Saint Eloi - CHU Montpellier, Montpellier, 34285 cedex 5, France|F?pital d'Instruction des Amées du Val de Grace, Paris, 75005, France|H?pital Cochin, Paris, 75014, France|H?pital Européen Georges Pompidou - Service d'oncologie médicale, Paris, 7505, France|Institut de Cancérologie Lucien Neuwirth, Saint Priest en Jarez, 42270, France|Centre Alexis Vautrin, Vandoeuvre-lès-nancy, 54511, France|Institut Gustave Roussy, Villejuif, 94805 cedex, France Less <<
NCT00436618 Leukemia|Lymphoma|Lymphoprolif... More >>erative Disorder Less << PHASE2 COMPLETED 2019-10-09 Mayo Clinic Scottsdale, Scotts... More >>dale, Arizona, 85259-5499, United States|Mayo Clinic - Jacksonville, Jacksonville, Florida, 32224, United States|Mayo Clinic Cancer Center, Rochester, Minnesota, 55905, United States Less <<
NCT00973713 Cholangiocarcinoma PHASE2 UNKNOWN 2025-03-12 Austin Health, Melbourne, Vict... More >>oria, 3084, Australia Less <<
NCT05252585 Renal Angiomyolipoma PHASE4 RECRUITING 2026-02-21 Novartis Investigative Site, T... More >>aichung, Taiwan ROC, 40201, Taiwan|Novartis Investigative Site, Taoyuan, Taiwan ROC, 33305, Taiwan|Novartis Investigative Site, Taipei, 10002, Taiwan Less <<
NCT01242631 Testicular Cancer|Germ Cell Ca... More >>ncer Less << PHASE2 COMPLETED 2025-03-14 Vivantes Klinikum am Urban, Be... More >>rlin, 10967, Germany|Universitatsklinikum Essen, Essen, 45122, Germany|Universitatsklinikum Hamburg-Eppendorf, Hamburg, 20246, Germany|Hannover Medical School, Hannover, 30625, Germany|Universitatsklinikum Schieswig-Holstein - Campus Kiel, Kiel, 24105, Germany|Universitatsklinikum Marburg, Marburg, 35043, Germany|Klinikum Harlaching München, München, 81545, Germany|Universitatsklinikum der Eberhard-Karls-Universitat Tübingen, Tübingen, 72076, Germany Less <<
NCT01931163 Breast Cancer|Triple Negative ... More >>Breast Cancer Less << PHASE2 COMPLETED 2025-01-19 The Methodist Hospital, Housto... More >>n, Texas, 77030, United States|Houston Methodist Hospital Willowbrook, Houston, Texas, 77070, United States|Houston Methodist Hospital Sugar Land, Sugar Land, Texas, 77479, United States Less <<
NCT06126588 Meningioma PHASE2 NOT_YET_RECRUITING 2028-05-01 CHRU of Nancy, Vand?uvre-lès-N... More >>ancy, Grand Est, 54511, France|Nancy Hospital, Vand?uvre-lès-Nancy, 54511, France Less <<

Protocol

Bio Calculators
Preparing Stock Solutions 1mg 5mg 10mg

1 mM

5 mM

10 mM

1.04mL

0.21mL

0.10mL

5.22mL

1.04mL

0.52mL

10.44mL

2.09mL

1.04mL

 

Historical Records

Categories